Judy Weisenberg, MD
Professor of Neurology, Division of Pediatric Neurology, Epilepsy Section
Co-Director Washington University Rett Spectrum Clinic
Washington University School of Medicine
Talk Title: An Aerial View of Genetic Targeted Therapies in Neurodevelopmental Disabilities in 2026: Progress, Pitfalls and Conundra
Abstract: In the past 2 decades, there have been dramatic advances in our understanding of the genetics of many forms of neurodevelopmental disability as well as our ability to diagnose and potential treatment strategies. This talk will focus on Dravet Syndrome and Rett Syndrome but also touch on other similar conditions and the current state of the clinical trials as well as lessons learned and ongoing challenges.
Host: Dr. Joe Dougherty